Updates
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All of the items I own are covered with breast milk; it’s on my clothes, bedsheets, even my phone. Its subtle sweetness occasionally attracts ... Read more
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Hemlibra Now Available to Patients in Developing Countries via Aid Program
Hemlibra (emicizumab), the sole approved prophylactic treatment for hemophilia A, is now available to patients in developing countries via the World Federation of Hemophilia (WFH) Humanitarian ... Read more -
Patients, Family and Friends to Take Part in Variety of Rare Disease Day Events Worldwide
Scores of events are afoot worldwide to mark Feb. 28, Rare Disease Day 2019. The activities aim to raise awareness about rare diseases and the millions ... Read more -
Preliminary Data Further Show MarzAA’s Potential to Prevent Bleedings
Clinical data from the ongoing Phase 2/3 trial data evaluating MarzAA (marzeptacog alfa activated) in patients with Hemophilia A or B with inhibitors ... Read more -
We Will Continue to Rebuild Our Lives
February 2014 proved to host the last bleed “MacDonald the Younger” faced thus far. The treatment plan created by our Hemophilia Treatment Center ... Read more
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Single Dose of Gene Therapy AMT-061 Proves Effective in Hemophilia B
A single administration of AMT-061, an investigational gene therapy for people with severe and ... -
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What Are the Things That Most Defines Us?
The following is a group activity I like to do in some of the ... -
To My Husband, the Father of My Daughter
To the father of my daughter, Thank you for being present from the very ... -
Higher Doses of Adynovate is Effective as Preventive Treatment for Hemophilia A, Trial Suggests
Maintaining high concentrations of Adynovate in the blood of hemophilia A patients decreases the number ... -
This Is Way Beyond My Understanding
My youngest son, wife, and I just returned from an appointment with our hematologist ...
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Europe’s CHMP Recommends Approval of Hemlibra to Treat Hemophilia A
News
Europe’s Committee for Medicinal Products for Human Use (CHMP) has issued a positive opinion supporting the approval of Hemlibra (emicizumab) for routine prophylaxis of bleeding episodes in hemophilia A patients with factor VIII inhibitors. Hemlibra is a humanized monoclonal antibody that ... Read more