Updates
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HHS Secretary Alex Azar Touts White House Efforts to Cure Rare Diseases
Despite skyrocketing healthcare costs, President Trump is committed to protecting the 30 million or so Americans with rare diseases and ensuring timely, affordable access ... Read more -
First 2 Adults with Severe Hemophilia A Respond Well to Gene Therapy in Clinical Trial
Bayer’s investigational gene therapy BAY 2599023 safely and effectively increased the levels of clotting factor VIII (FVIII) and prevented or lessened bleeding in the first two people ... Read more -
We Aren’t in Kansas Anymore
My wife is scheduled for surgery this week in Albuquerque, New Mexico. She will be in the hospital for one or two nights. We ... Read more -
How to Be Prepared This Holiday Season
The holiday season is in full swing, and with fewer shopping days, it will be upon us more quickly than usual. While we are ... Read more
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Your Joint Health Is Important Sponsored Post
Submitted by Takeda Every joint bleed matters 70% to 80% of all bleeds in ... -
Insurer Highmark Forges New Hemophilia Partnership Focused on Treatment, Management
As part of a new partnership focused on hemophilia treatment and management, members of ... -
Breaking into the Boys Club: Women with Hemophilia
Since hemophilia was discovered, it has been accepted as a male disease. No one ... -
Programmed Pump Infusions Aid in Care of Hemophilia A Patients After Surgery, Study Says
A programmable mini-pump able to provide regular doses after surgery of FVIIa to hemophilia ... -
Giving Thanks for the Blessings in My Life
A “6 Years Ago Today” moment popped up in my Facebook feed recently. The ... -
Lower-dose Preventive Therapy Reduced Bleeding Events in Thai Children with Hemophilia A, Study Shows
A lower dose of regular, preventive therapy with factor VIII concentrates was better at ...
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Europe’s CHMP Recommends Approval of Hemlibra to Treat Hemophilia A
News
Europe’s Committee for Medicinal Products for Human Use (CHMP) has issued a positive opinion supporting the approval of Hemlibra (emicizumab) for routine prophylaxis of bleeding episodes in hemophilia A patients with factor VIII inhibitors. Hemlibra is a humanized monoclonal antibody that ... Read more