Updates
-
-
Risk of Inhibitors with Nuwiq Similar to Plasma-derived Products in Untreated Hemophilia A Patients, Trial Shows
Adults and children with severe hemophilia A who are receiving Nuwiq (recombinant human coagulation factor VIII) as their first replacement therapy have a ... Read more -
Wanting More Won’t Stop My Family from Being Content Now
My son couldn’t walk, and placing him in a wheelchair proved to be impossible. Internal bleeding into a knee or ankle forced my “stinky ... Read more -
2019 Was Rough, So I’m Embracing a New Year
With 2019 behind us, it’s time for everyone to start anew and welcome 2020 into their lives. It’s hard to be fond of 2019 ... Read more -
Remembering the Diagnosis
I received an email from a friend I hadn’t heard from in some time. She told me that her nephew and his wife just ... Read more -
ASC Therapeutics Partners with Vigene for Manufacturing Support for Hemophilia A Gene Therapy Program
ASC Therapeutics is partnering with Vigene Biosciences to support the manufacturing process of its current and future gene therapy clinical platforms — including its ... Read more
-
Your Joint Health Is Important Sponsored Post
Submitted by Takeda Every joint bleed matters 70% to 80% of all bleeds in ... -
Women Get Inhibitors, Too, and Should Be Tested Regularly
Recently, I was browsing the website of the National Hemophilia Foundation and came across ... -
The Joys of an Occasional Reprieve
I’d been sick with acute respiratory troubles for almost a week. Not a minute ... -
Generation Bio Raises $110 Million for Non-viral Gene Therapy for Hemophilia A, Other Diseases
Generation Bio said it received $110 million in funding to bring its innovative, non-viral ... -
AMT-061 Increases FIX Activity, Prevents Bleeds in Severe Hemophilia B Patients, Phase 2b Data Show
A single infusion of AMT-061 (etranacogene dezaparvovec), uniQure’s experimental gene therapy for the treatment ... -
I’m Thankful for Lessons Learned
My family entered the hemophilia community more than 23 years ago with the birth ...
Subscribe to our mailing list
Get regular updates delivered to your email box.
Thanks! Please check your email for a confirmation email.
Europe’s CHMP Recommends Approval of Hemlibra to Treat Hemophilia A
News
Europe’s Committee for Medicinal Products for Human Use (CHMP) has issued a positive opinion supporting the approval of Hemlibra (emicizumab) for routine prophylaxis of bleeding episodes in hemophilia A patients with factor VIII inhibitors. Hemlibra is a humanized monoclonal antibody that ... Read more